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atidarsagene autotemcel
atidarsagene autotemcel
RxCUI 2677916
ingredient
Indicated for · 23
Brain Diseases
Brain Diseases, Metabolic
Brain Diseases, Metabolic, Inborn
Central Nervous System Diseases
Congenital, Hereditary, and Neonatal Diseases and Abnormalities
Demyelinating Diseases
Disease
Diseases, Life Phases, Behavior Mechanisms and Physiologic States
Genetic Diseases, Inborn
Hereditary Central Nervous System Demyelinating Diseases
Leukodystrophy, Metachromatic
Leukoencephalopathies
Lipid Metabolism Disorders
Lipid Metabolism, Inborn Errors
Lipidoses
Lysosomal Storage Diseases
Lysosomal Storage Diseases, Nervous System
Metabolic Diseases
Metabolism, Inborn Errors
Nervous System Diseases
Nutritional and Metabolic Diseases
Sphingolipidoses
Sulfatidosis